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FDA rejects second Sarepta drug for Duchenne muscular dystrophy

S arepta Therapeutics suffered a surprise setback on Monday when the Food and Drug Administration rejected its request to commercialize a second medicine to treat children with Duchenne Muscular Dystrophy, a rare hereditary muscle wasting disease. [19659003] In a statement, Sarepta said the FDA has refused to approve its medicine called Vyondys 53 because of the risk of intravenous infusion …

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